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Adeno-associated virus serotype rh10 vector encoding the human factor IX gene |
|---|---|
| Trade Name | |
| Orphan Indication | Hemophilia B |
| USA Market Approval | USA |
| USA Designation Date | 2015-08-25 00:00:00 |
| Sponsor | Dimension Therapeutics;840 Memorial Drive;Cambridge, Massachusetts, 02139 |
