antisense oligonucleotide targeted to human transthyretin (TTR) mRNA

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antisense oligonucleotide targeted to human transthyretin (TTR) mRNA
Trade Name
Orphan Indication Hereditary ATTR amyloidosis
USA Market Approval USA
USA Designation Date 2012-07-24 00:00:00
Sponsor Ionis Pharmaceuticals, Inc.;2855 Gazelle Court;Carlsbad, California, 92010
Related Access Program
Alnylam Pharmaceuticals – Amyloidosis, Hereditary, Transthyretin-Related Alnylam Pharmaceuticals – Amyloid Neuropathies, Familial Alnylam Pharmaceuticals – Familial Amyloid Polyneuropathies Alnylam Pharmaceuticals – Familial amyloid polyneuropathy