|
adeno-associated viral vector serotype 9 containing human N-acetylglucosaminidase alpha gene |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type IIIB (Sanfilippo B syndrome) |
| USA Market Approval | USA |
| USA Designation Date | 2012-12-27 00:00:00 |
| Sponsor | Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona |
