26 base synthetic single-stranded fully phosphorothioated 2′-O-methyl-RNA and DNA mixmer oligonucleotide-based compound

26 base synthetic single-stranded fully phosphorothioated 2′-O-methyl-RNA and DNA mixmer oligonucleotide-based compound
Trade Name
Orphan Indication Dravet Syndrome
EU Market Approval EU
EU Designation Date 2017-02-27 00:00:00
Sponsor Eirgen Pharma Limited
Related Access Program
M. Scott Perry – Dravet Syndrome M. Scott Perry – Dravet Syndrome University of Colorado, Denver – Dravet Syndrome Children’s Hospital Medical Center, Cincinnati – Dravet Syndrome