recombinant, adeno-associated virus serotype 2 vector carrying linear single-stranded AADC mRNA cDNA | |
---|---|
Trade Name | |
Orphan Indication | Aromatic amino acid decarboxylase deficiency |
USA Market Approval | USA |
USA Designation Date | 2016-06-08 00:00:00 |
Sponsor | Agilis Biotherapeutics, LLC;Kendall Square, 245 First Street;Cambridge, Massachusetts, 02142 |