|
Exon 51 specific phosphorothioate oligonucleotide |
|---|---|
| Trade Name | |
| Orphan Indication | Duchenne muscular dystrophy |
| USA Market Approval | USA |
| USA Designation Date | 2009-08-25 00:00:00 |
| Sponsor | BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 |
