Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene

Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene
Trade Name
Orphan Indication Mucopolysaccharidosis type IIIB (Sanfilippo B syndrome)
EU Market Approval EU
EU Designation Date 2017-01-12 00:00:00
Sponsor Abeona Therapeutics Europe SL