Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Vocimagene amiretrorepvec and flucytosine Glioblastoma Tocagen, Inc.;3030 Bunker Hill St.;San Diego, California, 92109 January 12, 2011
N-[(2S)-2,3-dihydroxypropyl]-3-[(2-fluoro-4-iodophenyl)amino] isonicotinamide hydrochloride Acute myeloid leukemia EMD Serono, Inc.;1 Technology Place;Rockland, Massachusetts, 02370 January 12, 2011
Anti-TCR murine monoclonal antibody (MAB, type IgM) Pediatric multiple sclerosis Tolera Therapeutics, Inc.;350 E. Michigan Ave.;Kalamazoo, Michigan, 49008 January 12, 2011
[AC3-yCD2(V)] and Flucytosine (5-FC XR) Glioblastoma multiforme Tocagen, Inc.;3030 Bunker Hill St.;San Diego, California, 92109 January 12, 2011
Dabrafenib Metastatic Melanoma Novartis Pharmaceuticals Corp.;One Health Plaza;East Hanover, New Jersey, 07936 January 12, 2011
Vocimagene amiretrorepvec and flucytosine Glioblastoma multiforme Tocagen, Inc.;3030 Bunker Hill St.;San Diego, California, 92109 January 12, 2011
4-[131I]iodo-L-phenylalanine Glioma Therapeia GmbH & Co KG;Veilchenweg 38, D-01326 Dresden; January 4, 2011
Bortezomib Follicular lymphoma Millennium Pharmaceuticals, Inc.;40 Landsdowne Street;Cambridge, Massachusetts, 02139 January 4, 2011
GVAX melanoma Metastatic Melanoma Aduro BioTech, Inc.;740 Heinz Avenue;Berkeley, California, 94710 December 23, 2010
Calcium benzoate and risperidone Pediatric patients with schizophrenia University of California, Los Angeles;Dept. of Psychiarty, HH212, 1000 W. Carson Street;Torrance, California, 90509 December 20, 2010
Ex-vivo expanded autologous bone marrow-derived mesenchymal stem cells Amyotrophic lateral sclerosis TCA Cellular Therapy, LLC;101 Judge Tanner Blvd.;Covington, Louisiana, 70433 December 20, 2010
Crenolanib Malignant glioma AROG Pharmaceuticals, LLC;12400 Coit Road, Suite 570;Dallas, TX, 75251 December 20, 2010
Crenolanib besylate Glioma AROG Pharmaceuticals, LLC;Two Lincoln Centre, Suite 410;Dallas, Texas, 75240 December 20, 2010
Denosumab Patients with giant cell tumor of bone Amgen, Inc.;One Amgen Center Drive;Thousand Oaks, California, 91320 December 20, 2010
Dinutuximab Neuroblastoma United Therapeutics Corporation;55 TW Alexander Drive;Research Triangle Park, North Carolina, 27709 December 20, 2010
NDX-peptides Amyotrophic lateral sclerosis NeoDiagnostic Research Ltd;Sheraton House 1st Floor, Chorleywood;Herts WD3 5LH December 14, 2010
DNA plasmid vector expressing eIF5Ak50 Multiple myeloma Senesco Technologies, Inc.;303 George Street;New Brunswick, New Jersey, 08901 December 13, 2010
Fidaxomicin Pediatric Clostridium difficile infection Cubist Pharmaceuticals LLC, a subsidiary of Merck & Co., Inc.;20 Weystrasse;Luzern December 13, 2010
Dermagraft Dystrophic epidermolysis bullosa Shire Regenerative Medicine, Inc.;11095 Torreyana Road, subsidiary of Shire Pharmaceuticals.;San Diego, California, 92121 December 13, 2010
Cediranib Glioblastoma National Institutes of Health;National Cancer Institute, 9609 Medical Center Dr.;Bethesda, Maryland, 20892 December 13, 2010
Acyclovir Herpetic keratitis Fera Pharmaceuticals;134 Birch Hill Road;Locust Valley, New York, 11560 December 13, 2010
(2E,4E,6Z,8E)-3,7-dimethyl-9-(2,6,6-trimethylcyclohex-1-enyl)nona-2,4,6,8-tetraenyl acetate 9-cis-retinyl acetate (API) Leber congenital amaurosis Novelion Therapeutics, Inc.;887 Great Northern Way - Suite 250, Vancouver, British Columbia;V5T 4T5 December 2, 2010
(2E, 4E, 6Z, 8E)-3,7-dimethyl-9-(2,6,6-trimethylcyclohex-1-en-l-yl) nona-2,4,6,8-tetraen-l-yl acetate Retinitis pigmentosa Novelion Therapeutics, Inc.;887 Great Northern Way - Suite 250, Vancouver, British Columbia, V5T 4T5; December 2, 2010
Allogeneic cord blood cells, ex vivo modulated with 16,16 dimethyl prostaglandin E2 (dmPGE2) Enhancement of stem cell engraftment through ex vivo treatment of human allogeneic hematopoietic stem cells (treatment of neuropenia, thrombocytopenia, lymphopenia, and anemia) Fate Therapeutics, Inc.;3535 General Atomics Court;San Diego, California, 92121 December 2, 2010
(Z)-9-{[2,2-bis-(hydroxymethyl)cyclopropylidene]methyl}guanine, cyclopropavir, ZSM-1-62 and NSC D745998 Active cytomegalovirus infections Microbiotix, Inc.;One Innovation Drive;Worcester, MA, 01605 November 29, 2010