Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

Become a Partner.

Country Product Indication Sponsor Date
Choline tetrathiomolybdate Wilson disease Wilson Therapeutics AB;Strandvagen 5b, 114 51 Stockholm, Sweden; August 25, 2011
Dinaciclib Chronic lymphocytic leukemia Merck Sharp & Dohme Ltd.;Hertford Road, Hoddesdon, Hertfordshire EN11 9BU; August 25, 2011
6,8-bis-benzylsulfanyl-octanoic acid Acute myeloid leukemia Cornerstone Pharmaceuticals, Inc.;25 Health Science Drive;Stony Brook, New Mexico, 11790 August 22, 2011
Corifungin Amebic meningoencephalitis Ctr for Discovery & Innovation in Parasitic Diseas;University of CA, San Francisco, Byers Hall Room 508B, QB3;San Francisco, California, 94158 August 22, 2011
Allogeneic ex-vivo expanded placental adherent stromal cells Buerger’s disease Novella Clinical, Inc.;MATAM Advanced Technology Park, Haifa 31905; August 22, 2011
Alpha-1 proteinase inhibitor (human) Patients with recent onset (<15 years)with Type 1A diabetes mellitus with residual beta-cell function Kamada, Ltd.;2 Holtzman Street;Rehovot July 28, 2011
1-(4-{4-amino-7-[1-(2-hydroxyethyl)-1H-pyrazol-4-yl]thieno[3,2-c]pyridine-3-yl}phenyl)-3-(3-fluorophenyl)urea) Acute myeloid leukemia AbbVie, Inc.;1 N Waukegan Road, AP34/RA72;North Chicago, Illinois, 60064 July 28, 2011
Corifungin Leishmaniasis Sandler Center for Drug Discovery;University of CA, San Francisco, 1700 4th Street;San Francisco, California, 94158 July 6, 2011
Botulism antitoxin heptavalent (A, B, C, D, E, F, G) (Equine) Botulism Cangene Corporation;155 Innovation Drive, Winnipeg, Manitoba R3T5Y3; June 29, 2011
Fibronectin Peptide Prevention of burn injury progression of acute, deep dermal burns in hospitalized patients NeoMatrix Therapeutics, Inc.;Long Island High Tech Incubator, 25 Health Sciences Drive;Stony Brook, New York, 11790 June 29, 2011
(6-maleimidocaproyl)hydrazone of doxorubicin Soft tissue sarcoma NantCell, Inc.;9920 Jefferson Boulevard;Culver City, California, 90232 June 29, 2011
Denileukin diftitox T-cell lymphoma Eisai, Inc.;155 Tice Blvd.;Woodcliff Lake, New Jersey, 5271 June 29, 2011
Ambroxol Gaucher disease Belrose Pharma, Inc.;500 College Road E, Suite 205;Princeton, New Jersey, 08540 June 29, 2011
IgG1 chimeric monoclonal antibody Multiple myeloma Immune System Therapeutics Ltd;Suite 1, Level 1, Ultimo, NW 2007; June 22, 2011
Cyclophosphamide Graft Versus Host Disease Accentia Biopharmaceuticals, Inc.;324 S. Hyde Park Avenue;Tampa, Florida, 33606 June 17, 2011
Cytochrome C, flavin mononucleotide and thiamin diphosphate Mitochondrial disorders NBI Pharmaceuticals, Inc.;c/o Neil & Co CPAs, 1184 N. 15th Ave., Suite 1;Bozeman, Montana, 59715 June 17, 2011
NanoDTPA(tm) Known or suspected cases of internal contamination with plutonium, americium, or curium Nanotherapeutics, Inc.;13859 Progress Blvd;Alachua, Florida, 32615 June 17, 2011
7-B-Hydroxy Cholesteryl-3-B-Oleate-Ester Gliomas Intsel Chimos SA;1 rue Royale, 91123 Saint-Cloud Cedex; June 15, 2011
12-A-p21 RAS(5-21). 12-C-p21 RAS(5-21). 12-D-p21 RAS(5-21). 12-Rp21 RAS(5-21). 12-S-p21 RAS(5-21). 12-V-p21 RAS(5-21). 13-D-p21 RAS(5-21) Pancreatic Cancer Targovax OY;Saukonpaadenranta 2;Helsinki June 7, 2011
Autologous neo-uninary conduit Bladder dysfunction requiring incontinent urinary diversion Tengion, Inc.;2900 Potshop Lane;East Norriton, Pennsylvania, 19403 June 7, 2011
Cyclophosphamide Systemic scleroderma Accentia Biopharmaceuticals, Inc.;324 South Hyde Avenue, Suite 350;Tampa, Florida, 33606 June 7, 2011
Exendin-(9-39) Congential hyperinsulinenic hypoglycemia and other causes of hyperinsulinemic hypoglycemia in adults and children The Children's Hospital of Philadelphia;Children's Hospital of Phil. Research Institute, Abramson Research Center;Philadelphia, Pennsylvania, 19104 June 1, 2011
Recombinant humanized anti-LOXL2 monoclonal antibody, IgG4(S241P) Myelofibrosis Gilead Sciences, Inc.;199 E. Blaine St.;Seattle, Washington, 98102 June 1, 2011
Ciprofloxacin Bronchiectasis Aradigm Corporation;3929 Point Eden Way;Hayward, California, 94545 June 1, 2011
Adeno-associated virus vector serotype 9 expressing human sulfamidase Mucopolysaccharidosis type IIIA (Sanfilippo A Syndrome) Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona June 1, 2011