Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

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Country Product Indication Sponsor Date
Cysteamine Nephropathic cystinosis Mylan Laboratories, Inc.;781 Chestnut Ridge Road, P.O. Box 4310;Morgantown, West Virginia, 26504 January 25, 1991
Ricin (blocked) conjugated murine MCA (n901) Small cell lung cancer ImmunoGen, Inc.;830 Winter Street;Waltham, Massachusetts, 02451 January 25, 1991
Ricin (blocked) conjugated murine mca (anti-b4) Acute lymphoblastic leukemia ImmunoGen, Inc.;830 Winter Street;Waltham, Massachusetts, 02451 January 24, 1991
Desmopressin acetate Hemophilia A Ferring Pharmaceuticals, Inc.;100 Interpace Parkway;Parsippany-Troy Hills, New Jersey, 07054 January 22, 1991
Testosterone sublingual Constitutional delay of growth and puberty in boys Bio-Technology General Corp.;70 Wood Avenue, South;Iselin, New Jersey, 08830 January 16, 1991
Dornase alfa Cystic fibrosis Genentech, Inc.;1 DNA Way;South San Francisco, California, 94080 January 16, 1991
Dronabinol For the stimulation of appetite and prevention of weight loss in patients with a confirmed diagnosis of AIDS Unimed Pharmaceuticals, Inc.;901 Sawyer Rd.;Marietta, Georgia, 30062 January 15, 1991
Mucoid exopolysaccharide Pseudomonas hyperimmune globulin Cystic fibrosis North American Biologicals, Inc.;12280 Wilkins Avenue;Rockville, Maryland, 20852 January 9, 1991
Cladribine Chronic lymphocytic leukemia Janssen Research & Development, LLC;Global Regulatory Affairs, 920 US Route 202;Raritan, New Jersey, 08869 December 31, 1990
3,4-diaminopyridine Lambert-Eaton Myasthenic Syndrome Jacobus Pharmaceutical Company;37 Cleveland Avenue, P.O. Box 5290;Princeton, New Jersey, 08540 December 18, 1990
Bovine colostrum AIDS-related diarrhea Hastings, Donald DVM;1030 North Parkview Drive;Bismarck, North Dakota, 58501 November 19, 1990
Microbubble contrast agent Intraoperative aid in the identification and localization of intracranial tumors Cav-Con, Inc.;55 Knollwood Road;Farmington, Connecticut, 06032 November 16, 1990
Cladribine Hairy cell leukemia R. W. Johnson Pharmaceutical Research Institute;Route 202, P.O. Box 300;Raritan, New Jersey, 08869 November 15, 1990
Filgrastim Chronic neutropenia Amgen, Inc.;1840 Dehavilland Drive;Thousand Oaks, California, 91320 November 7, 1990
Mucoid exopolysaccharide Pseudomonas hyperimmune globulin Cystic fibrosis North American Biologicals, Inc.;12280 Wilkins Avenue;Rockville, Maryland, 20852 November 7, 1990
Succimer Prevention of cystine kidney stone formation in patients with homozygous cystinuria who are prone to stone development Sanofi Winthrop, Inc.;90 Park Avenue;New York, New York, 10016 November 5, 1990
Calcitonin salmon nasal spray Paget disease Sandoz Pharmaceuticals Corp.;59 Route 10;East Hanover, New Jersey, 07936 October 29, 1990
Tretinoin Acute promyelocytic leukemia Hoffmann-La Roche, Inc.;340 Kingsland Street;Nutley, New Jersey, 07110 October 24, 1990
Gossypol Adrenal cancer Reidenberg, Marcus M. M.D.;The New York Hospital - Cornell Medical Center, 525 East 68th Street, Box 70;New York, New York, 10021 October 22, 1990
Taxol isolated from Taxus brevifolia Ovarian cancer Bristol-Myers Squibb;5 Research Parkway;Wallingford, Connecticut, 06492 October 15, 1990
Methotrexate with laurocapram Topical treatment of mycosis fungoides Echo Therapeutics, Ltd.;8 Penn Center, 1628 JFK Blvd;Philadelphia, Pennsylvania, 19103 October 15, 1990
Dextran sulfate (inhaled, aerosolized) For use as an adjunct to the treatment of cystic fibrosis Kennedy & Hoidal, M.D.'s;University of Utah Health Sciences Center, 50 North Medical Drive, Room 4R240;Salt Lake City, Utah, 84132 October 5, 1990
Oxandrolone Constitutional delay of growth and puberty Bio-Technology General Corp.;70 Wood Avenue, South;Iselin, New Jersey, 08830 October 5, 1990
Hydroxyurea Sickle cell anemia Bristol-Myers Squibb Pharmaceutical Research Institute;P.O. Box 4000;Princeton, New Jersey, 08543 October 1, 1990
Filgrastim Neutropenia associated with bone marrow transplants Amgen, Inc.;1840 Dehavilland Drive;Thousand Oaks, California, 91320 October 1, 1990