Disease: Tyrosinemia type 1
- A 12-month, longitudinal, intervention study examining a tablet protein substitute preparation in the management of tyrosinemia
- A case report of two siblings with hypertyrosinemia type 1 presenting with hepatic disease with different onset time and severity
- A False-Negative Newborn Screen for Tyrosinemia Type 1-Need for Re-Evaluation of Newborn Screening with Succinylacetone
- A Lithuanian Case of Tyrosinemia Type 1 with a Literature Review: A Rare Cause of Acute Liver Failure in Childhood
- A patient with urinary succinylacetone-negative hereditary tyrosinemia type 1
- A split prime editor with untethered reverse transcriptase and circular RNA template
- Activation of homology-directed DNA repair plays key role in CRISPR-mediated genome correction
- Adenine base editing and prime editing of chemically derived hepatic progenitors rescue genetic liver disease
- ADHD symptoms in neurometabolic diseases: Underlying mechanisms and clinical implications
- Adult female with severe decompensation of tyrosinaemia type 1 that responds to heme treatment
- Alkaptonuria - Past, present and future
- An engineered Escherichia coli Nissle strain prevents lethal liver injury in a mouse model of tyrosinemia type 1
- An Infant with Bilateral Keratitis: From Infectious to Genetic Diagnosis
- Application of machine learning tools and integrated OMICS for screening and diagnosis of inborn errors of metabolism
- Bilateral recurrent pseudodendritic keratopathy as the initial manifestation of tyrosinemia type II
- Biochemical and behavioural profile of NTBC treated Tyrosinemie type 1 mice
- Case report: ADHD and prognosis in tyrosinemia type 1
- Casein Glycomacropeptide: An Alternative Protein Substitute in Tyrosinemia Type I
- Clinical and biochemical footprints of inherited metabolic diseases. VIII. Neoplasias
- Clinical and genetic characteristics of two patients with tyrosinemia type 1 in Slovenia - A novel fumarylacetoacetate hydrolase (<em>FAH</em>) intronic disease-causing variant
- Clinical and genetic characteristics of two patients with tyrosinemia type 1 in Slovenia - A novel fumarylacetoacetate hydrolase (FAH) intronic disease-causing variant
- Clinical experience with hepatorenal tyrosinemia from a single Egyptian center
- Clinical features and genetic analysis of a child with acute form of Tyrosinemia type I due to a novel variant of FAH gene
- Clinical Spectrum of Hereditary Tyrosinemia Type 1 in a Cohort of Pakistani Children
- Comprehensive Evaluation of the NeoBase 2 Non-derivatized MSMS Assay and Exploration of Analytes With Significantly Different Concentrations Between Term and Preterm Neonates
- Consenso mexicano de tirosinemia tipo 1
- Corneal Crystals in Patients With Tyrosinemia Types I and II
- Current Landscape on Development of Phenylalanine and Toxicity of its Metabolites - A Review
- Current Landscape on Development of Phenylalanine and Toxicity of its Metabolites- A Review
- Decoding hepatorenal tyrosinemia type 1: Unraveling the impact of early detection, NTBC, and the role of liver transplantation
- Determinants of tyrosinaemia during nitisinone therapy in alkaptonuria
- Development of Flow Injection Analysis Method for the Second-Tier Estimation of Succinylacetone in Dried Blood Spot of Newborn Screening
- Diagnosis of inborn errors of metabolism within the expanded newborn screening in the Madrid region
- Diagnostic and Therapeutic Challenges of Hereditary Tyrosinemia Type 1 in Lebanon: A 12-Year Retrospective Review
- E. coli´s fight against TYROnny: Designing a bacterial strain to tackle tyrosinemia type 1
- E. colis fight against TYROnny: Designing a bacterial strain to tackle tyrosinemia type 1
- Efficient expansion and CRISPR-Cas9-mediated gene correction of patient-derived hepatocytes for treatment of inherited liver diseases
- Electronic structure and molecular properties of nitisinone and mesotrione in water
- Emotional and behavioural functioning in children with tyrosinaemia type 1
- Engineering a transposon-associated TnpB-ωRNA system for efficient gene editing and phenotypic correction of a tyrosinaemia mouse model
- Evaluation of a New 'Mix-In' Style Glycomacropeptide-Based Protein Substitute for Food and Drinks in Patients with Phenylketonuria and Tyrosinemia
- Evaluation of dynamic thiol/disulfide homeostasis in hereditary tyrosinemia type 1 patients
- Evaluation of surgical strategies and long-term outcomes in pediatric hepatocellular carcinoma
- Ex vivo gene editing and cell therapy for hereditary tyrosinemia type 1
- Family planning decisional needs assessment for recessive hereditary disorders: Insights from carrier couples and professionals
- Fumarylacetoacetate hydrolase gene as a knockout target for hepatic chimerism and donor liver production
- Generation of an induced pluripotent stem cell line SDQLCHi026-A from a hereditary tyrosinemia type I patient carrying compound heterozygote mutations in FAH gene
- Generation of immunodeficient pig with hereditary tyrosinemia type 1 and their preliminary application for humanized liver
- Hepatocellular carcinoma requiring liver transplantation in hereditary tyrosinemia type 1 despite nitisinone therapy and alpha1-fetoprotein normalization
- Hepatocellular carcinoma requiring liver transplantation in hereditary tyrosinemia type 1 despite nitisinone therapy and α1-fetoprotein normalization
- Hereditary tyrosinaemia type 1 in the absence of succinylacetone: 4-oxo 6-hydroxyhepanoate (4OHHA), a putative diagnostic biomarker
- Hereditary Tyrosinemia Type 1 in Jordan: A Retrospective Study
- Hereditary Tyrosinemia Type 1 Mice under Continuous Nitisinone Treatment Display Remnants of an Uncorrected Liver Disease Phenotype
- Hereditary tyrosinemia type Ⅰ: newborn screening, diagnosis and treatment
- Hereditary Tyrosinemia Type-1 With Late Presentation: A Case Report
- Hypertyrosinemia
- Hypertyrosinemia
- Identification and functional characterization of a novel homozygous intronic variant in the fumarylacetoacetate hydrolase gene in a Chinese patient with tyrosinemia type 1
- Improved specificity and efficacy of base-editing therapies with hybrid guide RNAs
- In vivo dissection of the mouse tyrosine catabolic pathway with CRISPR-Cas9 identifies modifier genes affecting hereditary tyrosinemia type 1
- In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
- Influence of nitisinone and its metabolites on l-tyrosine metabolism in a model system
- Initial presentation, management and follow-up data of 33 treated patients with hereditary tyrosinemia type 1 in the absence of newborn screening
- Liver Transplantation for Tyrosinemia Type 1 in the Developing World: Is It Really the Best We Can Offer?
- Liver Transplantation for Tyrosinemia Type 1 in the Developing World: Is It Really the Best We Can Offer?: Authors' Reply
- Liver Transplantation for Tyrosinemia Type 1 in the Developing World: Is It Really the Best We Can Offer?: Correspondence
- Liver Transplantation: A Safe and Definitive Alternative to Lifelong Nitisinone for Tyrosinemia Type 1
- Long-term safety and outcomes in hereditary tyrosinaemia type 1 with nitisinone treatment: a 15-year non-interventional, multicentre study
- Maleic acid is a biomarker for maleylacetoacetate isomerase deficiency; implications for newborn screening of tyrosinemia type 1
- Modified by the Innovative Drugs and Strategies-Pattern of Selected Indications for Pediatric Liver Transplantation
- mRNA-based therapy proves superior to the standard of care for treating hereditary tyrosinemia 1 in a mouse model
- Neonatal hyperinsulinism in transient and classical forms of tyrosinemia
- Neurocognitive outcome and mental health in children with tyrosinemia type 1 and phenylketonuria: A comparison between two genetic disorders affecting the same metabolic pathway
- Nitisinone
- Nitisinone
- Nitisinone treatment during two pregnancies and breastfeeding in a woman with tyrosinemia type 1 - a case report
- Nitisinone: two decades treating hereditary tyrosinaemia type 1
- Novel HPD mutation p.A244V compound with p.T219M causing tyrosinemia type III in a Chinese girl and review of the genotype-phenotype spectrum
- NTBC Treatment Monitoring in Chilean Patients with Tyrosinemia Type 1 and Its Association with Biochemical Parameters and Liver Biomarkers
- Nutritional interventions for patients with alkaptonuria: A minireview
- Outcome of Tyrosinemia Type 1 in Indian Children
- Physical Growth of Patients with Hereditary Tyrosinaemia Type I: A Single-Centre Retrospective Study
- Revitalizing liver function in mice with liver failure through transplantation of 3D-bioprinted liver with expanded primary hepatocytes
- Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
- Short-term nitisinone discontinuation of hereditary tyrosinemia type 1 mice causes metabolic alterations in glutathione metabolism/biosynthesis and multiple amino acid degradation pathways
- Simultaneous newborn screening for sickle cell disease, biotinidase deficiency, and hereditary tyrosinemia type 1 with an optimized tandem mass spectrometry protocol
- Structure-based discovery of pyrazole-benzothiadiazole hybrid as human HPPD inhibitors
- Syndrome of Inappropriate Antidiuretic Hormone Secretion in a Patient with Uncontrolled Tyrosinaemia Type 1
- The clinical variations and diagnostic challenges of deoxyguanosine kinase deficiency: a descriptive case series
- The compound heterozygous mutations of c.607G>a and c.657delC in the FAH gene are associated with renal damage with hereditary tyrosinemia type 1 (HT1)
- The compound heterozygous mutations of c.607G>a and c.657delC in the FAH gene are associated with renal damage with hereditary tyrosinemia type 1 (HT1)
- The effects of phenylalanine and tyrosine levels on dopamine production in rat PC12 cells. Implications for treatment of phenylketonuria, tyrosinemia type 1 and comorbid neurodevelopmental disorders
- The mutation spectrum and ethnic distribution of non-hepatorenal tyrosinemia (types II, III)
- Therapeutic Targeting of Fumaryl Acetoacetate Hydrolase in Hereditary Tyrosinemia Type I
- Treatment adherence in tyrosinemia type 1 patients
- Tyrosine catabolites influence SKN-1 signaling in a model of Type I Tyrosinemia
- Tyrosinemia type 1 in pediatric nephrology: Not always straightforward
- UK Dietary Practices for Tyrosinaemias: Time for Change
- UK should screen for tyrosinaemia in newborn babies, committee recommends
- Update on pathogenesis, diagnosis and treatment of hereditary tyrosinemia type Ⅰ