US Conference on Rare Diseases & Orphan Products

The Meeting For All Stakeholders in the Rare Disease/Orphan Product Community

The US Conference on Rare Diseases & Orphan Products – Shaping the Future Now – annual meeting where stakeholders – patients, patient organizations, researchers, drug and device companies, investors, thought leaders and government – meet to focus on rare diseases and orphan product research, development and access. At this year’s meeting, we seek to gain a common understanding of the current and emerging challenges, opportunities, and strategies for working together effectively to shape a better future for rare diseases and orphan drugs. It is important to remember none of us can get there alone. The 2011 meeting brought together more than 300 stakeholders, and this year’s event promises even more.

The format of the meeting includes both plenary and smaller group sessions. High-level plenary sessions will open a collaborative dialogue among leading researchers, company officials, investors, patient organizations and government leaders. Smaller group sessions are organized around three central themes: policy, research and regulation and special challenges. These sessions are intended to promote advancements in science, care and other considerations that will address the needs of the 30 million Americans with rare diseases. Topics include the current and emerging drug development environment, reenactment of the Prescription Drug and Medical Device User Fee Act, an update on NIH’s new National Center Advancing Translational Science, and many others.




Tabletop Exhibit Information

Attendees may visit the tabletop exhibits during the event and receptions.


Shannon Lewis Exhibits Associate

Phone +1.215.442.6149

Fax +1.215.442.6199

Email [email protected]


Event Information


Carrie Dunn

Program Developer

Phone +1. 215.442.6181

Fax +1.215.442.6199E

Email [email protected]