US Conference on Rare Disease and Orphan Drugs

Join all stakeholders—patients, researchers, companies, investors, thought leaders and government—for a unique opportunity for all who are focused on rare diseases to gain a common understanding of the previous and emerging challenges and opportunities and strategies for the future. View program


Take advantage of separate tracks for patients, researchers, companies, and investors, in addition to high-level plenary sessions where leading researchers, company officials, patient organizations and government leaders will discuss how the various interests can collaborate more productively. View program



  • Researchers from academia and drug and device companies
  • Patient organizations and those interested in creating one
  • Senior managers from drug and device companies interested in rare diseases
  • Investors focused on the future of orphan product development
  • Policy experts who are concerned about federal or state policies that affect patients with rare diseases
  • Providers of services to the rare disease community, including insurance providers and health care professionals
  • Government officials responsible for rare disease research and orphan product oversight

Register now to reserve your place at the conference.