Don’t miss the opportunity to hear these exciting Business Forum presentations by pediatric institutions.
- Rare Disease Partnering Summit: Presentations 2:00 – 5:00 pm
- Rare Disease Partnering Summit Reception, sponsored by Shire: 5:00 – 6:00 pm
Join renowned investigators from five world-class pediatric institutions on April 24 from 2-5pm as they present translational research projects and partnering opportunities that focus on rare diseases. The Rare Disease Partnering Summit is designed to facilitate collaboration with industry and advance research in rare and orphan diseases. A networking reception will follow at 5pm. Participating institutions include Boston Children’s Hospital, Cincinnati Children’s Hospital, Children’s Hospital Los Angeles, The Hospital for Sick Children, Toronto and University of Chicago Comer Children’s Hospital.
Open to all attendees.
Rare Disease Partnering Summit Presentations 2:00 – 5:00 pm
2:00 pm Introduction from Shire
2:05 – 2:35 pm
Boston Children’s
David Margulies, MD
Title: Towards Precision Care
Clifford Woolf, MD, PhD
Title: Stem Cell Derived Human Neurons For Modeling Disease and Drug Screening
Bruce Trapnell, MD
3:15 – 3:45 pm
Barry Maurer, MD, PhD
3:50 – 4:30 pm
University of Chicago Comer Children’s
Erika Claud, MD
Title: TBD
Beth McNally, MD, PhD
Title: TBD
4:25 – 4:55 pm
Toronto SickKids
Peter Dirks, MD, PhD
Title: Dissecting Brain Tumor Heterogeneity: Implications for Novel Novel Therapies
Don Mahuran, PhD
Title: Small Molecule Therapy for Lysosomal Storage Diseases
For more infotmation visit http://convention.bio.org/rare-diseases-partnering-summit/