This new meeting (International Conference on Sarcoma Biology) will interface with the Milan translational sarcoma meeting, in that the Milan meeting organizers will provide feedback on the proposed programs, and they will participate (as attendees) in the sarcoma biology meeting. The aim of the International Conference on Sarcoma Biology is...
Events
Several of the symposia and/or individual presentations within the symposia are expected to be published in the refereed literature, especially in Environmental Molecular Mutagenesis or Mutation Research. In additions, the interactions among the numerous highly experienced researchers who will attend this meeting are expected to generate collaborations that will substantially...
The goals of the Working Group are to identify research priorities for translational II research in sickle cell disease. The Working Group is designed to foster cross-disciplinary communication and to ensure that other disciplines and skill sets are included in sickle cell research. These priorities—the study designs, methods, disciplines, and...
The conference in 2009 will be the first opportunity to present and discuss results from the initial TSC clinical trials and additional data from basic research and to discuss plans for new clinical trials utilizing mTOR inhibitors and other drug targets. There are significant research opportunities to be discussed and...
Conference goals are to (a) provide a better awareness and harmonization of the diagnostic criteria of the disease and cofactors that contribute to the evolution of clinical disease associated with the defined genetic defects of autoimmune lymphoproliferative syndrome (ALPS) in the hematology, oncology, immunology, and infectious disease community; (b) establish...
Following this 2-day summit, a subset of attendees will provide recommendations for GenTAC for future directions. In addition, the National Marfan Foundation will sponsor a meeting that will focus on the use of information discussed at the meeting to derive a plan for the future development of therapeutic strategies for...
The goals of this meeting are to (1) develop a consensus set of diagnostic criteria for PFAPA, (2) deepen our understanding of the immunobiology of PFAPA, (3) possibly organize a consortium for GWAS in PFAPA, and (4) develop a multicenter treatment protocol for PFAPA. We expect that the meeting will...
The SMS Research Roundtable Symposia will be held in conjunction with the Sixth International Family Conference on Smith-Magenis Syndrome, “Building Bridges of Hope,” on September 17-20, 2009. The Research Roundtable commences the conference and fosters the partnership between parents and researchers, which directly supports the PRISMS’ mission. The Research Roundtable...
This meeting will bring together individuals involved with conveying complex information to different types of audiences. We hope to engage the audience in discussing issues around defining information quality, choosing content appropriately, and utilizing new technologies effectively for education. The audience will include individuals interested in education, evidence-based care, communication,...
Sickle Cell Disease is an inherited condition characterized by severe bone pains, anemia, recurrent infections and complications of the major organs of the body. This condition is inherited and can be prevented if individuals and the community as a whole take testing seriously. Testing for sickle cell disease carrier state...
EMERGING COMMERCIALIZATION STRATEGIES FOR ADDRESSING THE NEEDS OF ULTRA ORPHAN PATIENTS Accelerate Product Launch and Profitability by Building Regulatory Requirements into Distribution http://www.centrichealthresources.com/2009Conference/ The recent Risk Evaluation and Mitigation Strategies (REMS) requirements implemented by the Food and Drug Administration Amendments Act (FDAAA) have made the drug approval process more challenging...
Understand the Latest Regulatory Policy, Clinical Strategies, Patient Outreach and Commercialization Dynamics Impacting Orphan Drug Development. This annual summit brings together industry stakeholders and key thought leaders in the rare disease and orphan drug development arena. Hear from the FDA on results from the “Science of Small Clinical Trials” eight...
The goal of this meeting is to allow interested individuals to express their opinions about the directions clinical research in thalassemia should take, given past experiences and limitations imposed by NIH budgets and regulatory requirements. These proceedings will also serve as the basis of a Request for Applications (RFA) for...
The objectives of this symposium are to (1) describe the latest findings regarding mitochondrial diseases; (2) share research findings and award new research grants; (3) explore the clinical manifestations of mitochondrial disorders, including diagnosis and treatment considerations, and understand the concepts of mitochondrial disease therapy; and (4) evaluate the links...
The first objective of this conference is to facilitate continued discussion and team building of pediatric hematopoietic cell transplant physicians and pediatric immunologists to work together to develop a North American consortium for treatment of children with PID. The workshop of May 2008 set in motion an important collaborative effort....
The primary focus will be on validated endpoints that are ready for incorporation into clinical trials now or in the near future and on methods to address confounding issues unique to studies of acute GVHD. These will be used by the NHLBI-sponsored Blood and Marrow Transplant Clinical Trials Network (BMT...
The goals of this workshop are to refine the meta-analysis done by the IEDB team and to identify knowledge gaps and further research opportunities. Prior meta-analyses meetings have successfully accomplished both. Epitope information will be examined to identify protective immune responses as well as those that may contribute to disease...
The intent of the meeting is to advance the overall field of cardiovascular development and congenital heart disease through the sharing of information and the facilitation of collaborative investigations. An additional goal is to aid the career development of students, postdoctoral fellows, and junior faculty members by providing a forum...
The CIS Primary Immune Deficiency Consortium Conference will provide new investigators in this field the continued opportunity to enhance career development by learning from leaders in the field of primary immunodeficiency and other young investigators from institutions across the Americas and Europe.