Pompe & Pain – Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease

Spinal muscular atrophy- type 3

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab-ONYX The Effect of Aerobic Exercise Training in Patients With Type III Spinal Muscular Atrophy Spinal Cord Stimulation in Spinal Muscular Atrophy Pompe & Pain – Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease Phase 3 Active Treatment Trial to Evaluate the Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Who Are Being Treated With Nusinersen or Risdiplam Low Interventional Pilot Study to Assess Musculoskeletal Nociceptive Pain in Participants With Neuromuscular Disorders Spinraza in Adult Spinal Muscular Atrophy Safety and Efficacy of Olesoxime (TRO19622) in 3-25 Years SMA Patients. SPACE Trial: Pyridostigmine vs Placebo in SMA Types 2, 3 and 4 An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy Safety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 Motor Development and Orthoses in Spinal Muscular Atrophy (SMA) Aerobic Training in Patients With Spinal Muscular Atrophy Type III Whole Body Vibration Therapy in Children With Spinal Muscular Atrophy Wearable Technology to Assess Gait Function in SMA and DMD Oxidative Capacity and Exercise Tolerance in Ambulatory SMA Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III