Combined Malonic and Methylmalonic Aciduria (CMAMMA): Gene Identification and Outcome Study

Methylmalonic acidemia

Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in the mRNA-3705-P101 Study Combined Malonic and Methylmalonic Aciduria (CMAMMA): Gene Identification and Outcome Study