Bioavailability Food-Effect Study of an Oral Nitisinone Formulation to Treat Hereditary Tyrosinemia (HT-1)

Tyrosinemia type 1

Taste and Palatability of Orfadin Suspension Bioequivalence Study of Two Nitisinone Formulations Compared to Orfadin Bio Equivalency 20 Mgm Orfadin and 20 Mgm of Nitisonine Bioavailability Food-Effect Study of an Oral Nitisinone Formulation to Treat Hereditary Tyrosinemia (HT-1) Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 Biomarker for the Early Diagnosis and Monitoring in Tyrosinemia Type 1 (BioTyrosin) Hereditary Hepatorenal Tyrosinemia Natural History in Egypt and the Arab World (Multicenter Clinical Study) Phase II Study of the Enzyme Inhibitor NTBC for Tyrosinemia Type I Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care Evaluation of TYR Sphere Bioequivalence Study of Two Oral Nitisinone Formulations to Treat Hereditary Tyrosinemia (HT-1)