Angelman Syndrome (AS) Biomarker Study

Angelman syndrome

Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype Angelman Syndrome Video Assessment (ASVA) Source Material Study The Global Angelman Syndrome Registry HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome Angelman Syndrome Natural History Study- FAST UK A Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants Angelman Syndrome Natural History Study A Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome Study to Evaluate the Efficacy and Safety of Minocycline in Angelman Syndrome A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome A Study in Adults and Adolescents With Angelman Syndrome Angelman Syndrome (AS) Biomarker Study An Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman Syndrome Characterization of Angelman Syndrome Nutritional Formulation for Angelman Syndrome Study on Tolerability of Levodopa/Carbidopa in Children With Angelman Syndrome A Trial of Levodopa in Angelman Syndrome Minocycline in the Treatment of Angelman Syndrome Angelman Syndrome Italian Registry