A Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome

Angelman syndrome

Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype Angelman Syndrome Video Assessment (ASVA) Source Material Study The Global Angelman Syndrome Registry HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome Angelman Syndrome Natural History Study- FAST UK A Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants Angelman Syndrome Natural History Study A Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome Study to Evaluate the Efficacy and Safety of Minocycline in Angelman Syndrome A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome A Study in Adults and Adolescents With Angelman Syndrome Angelman Syndrome (AS) Biomarker Study An Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman Syndrome A Trial of Levodopa in Angelman Syndrome Characterization of Angelman Syndrome Nutritional Formulation for Angelman Syndrome Study on Tolerability of Levodopa/Carbidopa in Children With Angelman Syndrome Minocycline in the Treatment of Angelman Syndrome Angelman Syndrome Italian Registry