A Study of AAV9 Gene Therapy in Participants With Canavan Disease

Canavan disease

Canavan-Single Patient IND A Study of AAV9 Gene Therapy in Participants With Canavan Disease rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease GTA-Glyceryltriacetate for Canavan Disease Lithium and Acetate for Canavan Disease Oral Glyceryl Triacetate (GTA) in Newborns With Canavan Natural History Study of Patients With Canavan Disease, CAN Inform A Natural History Study of Canavan Disease