Gerard Vockley, MD, PhD – Glucose Transporter 1 Deficiency Syndrome

Submitted By:
Published Date:
January 25, 2020

Access Program Information

This treatment plan is intended for the use of UX007 (triheptanoin) in the treatment of a
single patient with Glucose Transporter 1 (GLUT1) Deficiency Syndrome.

Rare Disease:
Ohtahara syndrome