Limb Girdle Muscular Dystrophy Type 2E Recruitment Study

Limb-girdle muscular dystrophy- type 2E

A Study of the Natural History of Patients With LGMD2E, LGMD2D, and LGMD2C, ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD) Limb Girdle Muscular Dystrophy Type 2E Recruitment Study Gene Delivery Clinical Trial of SRP-9003 for Patients With LGMD2E (Beta-sarcoglycan Deficiency)