voretigene neparvovec-rzyl

voretigene neparvovec-rzyl
Trade Name Luxturna
Orphan Indication Inherited retinal dystrophy due to biallelic RPE65 gene mutations
USA Market Approval USA
USA Designation Date 2015-03-18 00:00:00
Sponsor Spark Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104