voretigene neparvovec-rzyl | |
---|---|
Trade Name | Luxturna |
Orphan Indication | Inherited retinal dystrophy due to biallelic RPE65 gene mutations |
USA Market Approval | USA |
USA Designation Date | 2015-03-18 00:00:00 |
Sponsor | Spark Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104 |