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Synthetic double-stranded oligomer specific to theSERPINA1gene and containing a cholesterol-conjugated, acyclic nucleobase analogue |
|---|---|
| Trade Name | |
| Orphan Indication | Congenital alpha-1 antitrypsin deficiency |
| EU Market Approval | EU |
| EU Designation Date | 2016-01-11 00:00:00 |
| Sponsor | Pharma Gateway AB |
