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Adeno-associated viral vector differentially expressing microdystrophin 5 gene via the muscle-specific promoter CK8 (rAAV9-CK8-h-�D5) |
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| Trade Name | |
| Orphan Indication | Duchenne muscular dystrophy |
| USA Market Approval | USA |
| USA Designation Date | 2016-08-31 00:00:00 |
| Sponsor | Solid GT, LLC;161 First Street, Suite 3A;Cambridge, Massachusetts, 02142 |
