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Modified messenger ribonucleic acid encoding human argininosuccinate lyase enzyme encapsulated into lipid nanoparticles |
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| Trade Name | |
| Orphan Indication | Argininosuccinic Aciduria |
| EU Market Approval | EU |
| EU Designation Date | 2017-12-12 00:00:00 |
| Sponsor | PhaseRx Ireland, Ltd |
