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anti-sense oligonucleotide consisting of 2�0-Me RNA with a phosphorothioate backbone |
|---|---|
| Trade Name | |
| Orphan Indication | Cystic fibrosis |
| USA Market Approval | USA |
| USA Designation Date | 2013-09-23 00:00:00 |
| Sponsor | ProQR Therapeutics III B.V.;Zernikedreef 9, 2333 CK Leiden, The Netherlands; |
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