Recombinant adeno-associated virus serotype 9 vector expressing codon-optimized miniaturized version of DMD gene | |
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Trade Name | |
Orphan Indication | Duchenne muscular dystrophy |
USA Market Approval | USA |
USA Designation Date | 2017-05-22 00:00:00 |
Sponsor | Bamboo Therapeutics, w wholly owned subsidiary of Pfizer;Worldwide Safety & Regulatory, Pfizer Inc.;Groton, Connecticut, 06340 |