This international conference provides a unique focus on the challenges facing therapy development for inherited neuromuscular diseases.
The conference sessions will look at the range of issues involved in therapy development in inherited neuromuscular diseases as well as discussing the lastest research developments in this area. Sessions will include:
- Natural History
- Desigining Effective Clinical Trials
- Biomarkers
- Platform Technologies
- Diagnosis and Care
- Delivering Therapeutics
- The Patient Voice
- Ethics and Society
For more information and registration please visit the Conference Website