Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene | |
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Trade Name | |
Orphan Indication | Mucopolysaccharidosis type IIIB (Sanfilippo B syndrome) |
EU Market Approval | EU |
EU Designation Date | 2017-01-12 00:00:00 |
Sponsor | Abeona Therapeutics Europe SL |