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Self-complementary adeno-associated viral vector serotype 9 containing theSGSHgene |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type IIIA (Sanfilippo A syndrome) |
| EU Market Approval | EU |
| EU Designation Date | 2016-10-14 00:00:00 |
| Sponsor | Abeona Therapeutics Europe SL |
