Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA | |
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Trade Name | |
Orphan Indication | Mucopolysaccharidosis type IIIA (Sanfilippo A syndrome) |
EU Market Approval | EU |
EU Designation Date | 2014-12-16 00:00:00 |
Sponsor | LYSOGENE |