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Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type IIIA (Sanfilippo A syndrome) |
| EU Market Approval | EU |
| EU Designation Date | 2014-12-16 00:00:00 |
| Sponsor | LYSOGENE |
