Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA

Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA
Trade Name
Orphan Indication Mucopolysaccharidosis type IIIA (Sanfilippo A syndrome)
EU Market Approval EU
EU Designation Date 2014-12-16 00:00:00
Sponsor LYSOGENE