 |
recombinant adeno-associated virus vector serotype 9 expressing human N-Sulfoglucosamine Sulfohydrolase |
|---|---|
| Trade Name | |
| Orphan Indication | Sanfilippo Syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2016-09-01 00:00:00 |
| Sponsor | Research Institute at Nationwide Children's Hospital;Center for Gene Therapy, 700 Childrens Drive;Columbus, Ohio, 43205 |
