|
chimeric fusion protein of recombinant human alpha-N-acetylglucosaminidase and human insulin-like growth factor 2 |
|---|---|
| Trade Name | |
| Orphan Indication | Sanfilippo Syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2014-11-25 00:00:00 |
| Sponsor | BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 |
