chimeric fusion protein of recombinant human alpha-N-acetylglucosaminidase and human insulin-like growth factor 2

chimeric fusion protein of recombinant human alpha-N-acetylglucosaminidase and human insulin-like growth factor 2
Trade Name
Orphan Indication Sanfilippo Syndrome
USA Market Approval USA
USA Designation Date 2014-11-25 00:00:00
Sponsor BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949