adeno-associated virus vector serotype 9 expressing human sulfamidase

adeno-associated virus vector serotype 9 expressing human sulfamidase
Trade Name
Orphan Indication Mucopolysaccharidosis type IIIA (Sanfilippo A Syndrome)
USA Market Approval USA
USA Designation Date 2011-06-01 00:00:00
Sponsor Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona