|
adeno-associated virus vector serotype 9 expressing human sulfamidase |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type IIIA (Sanfilippo A Syndrome) |
| USA Market Approval | USA |
| USA Designation Date | 2011-06-01 00:00:00 |
| Sponsor | Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona |
