|
adeno-associated virus vector encoding the SQ variant of human blood clotting factor VIII |
|---|---|
| Trade Name | |
| Orphan Indication | Hemophilia A |
| USA Market Approval | USA |
| USA Designation Date | 2016-02-29 00:00:00 |
| Sponsor | BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 |
