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adeno-associated viral vector type 2 expressing human recombinant retinal pigment epithelial 65KDa protein gene |
|---|---|
| Trade Name | |
| Orphan Indication | Inherited retinal dystrophy due to biallelic RPE65 gene mutations |
| USA Market Approval | USA |
| USA Designation Date | 2015-03-18 00:00:00 |
| Sponsor | Spark Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104 |
