adeno-associated viral vector serotype 9 containing human N-acetylglucosaminidase alpha gene | |
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Trade Name | |
Orphan Indication | Mucopolysaccharidosis type IIIB (Sanfilippo B syndrome) |
USA Market Approval | USA |
USA Designation Date | 2012-12-27 00:00:00 |
Sponsor | Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona |