adeno-associated viral vector serotype 9 containing human N-acetylglucosaminidase alpha gene

adeno-associated viral vector serotype 9 containing human N-acetylglucosaminidase alpha gene
Trade Name
Orphan Indication Mucopolysaccharidosis type IIIB (Sanfilippo B syndrome)
USA Market Approval USA
USA Designation Date 2012-12-27 00:00:00
Sponsor Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona