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Adeno-associated viral vector serotype 5 containing human ABCA4 gene |
|---|---|
| Trade Name | |
| Orphan Indication | Stargardt's disease |
| USA Market Approval | USA |
| USA Designation Date | 2008-09-30 00:00:00 |
| Sponsor | Fondazione Telethon;Via Varese 16 - 00185 Roma; |
|
Adeno-associated viral vector serotype 5 containing human ABCA4 gene |
|---|---|
| Trade Name | |
| Orphan Indication | Stargardt's disease |
| USA Market Approval | USA |
| USA Designation Date | 2008-09-30 00:00:00 |
| Sponsor | Fondazione Telethon;Via Varese 16 - 00185 Roma; |