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aadeno-associated viral vector, serotype 2, containing the human choroideremia gene encoding human Rab escort protein 1 |
|---|---|
| Trade Name | |
| Orphan Indication | Choroideremia |
| USA Market Approval | USA |
| USA Designation Date | 2013-09-12 00:00:00 |
| Sponsor | Sparks Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104 |
