adeno-associated virus type 8 delivering a vector genome with human retinoschisin promoter (RS/IRBP) and the human retinoschisin cDNA (hRS) | |
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Trade Name | |
Orphan Indication | X-linked Juvenile Retinoschisis |
USA Market Approval | USA |
USA Designation Date | 2015-11-16 00:00:00 |
Sponsor | Paul A. Sievig, MD, PhD, National Eye Institute, NIH;31 Center Drive, Bldg 31, Room 6A03;Bethesda, Maryland, 20892 |