Recombinant adeno-associated viral vector encoding a human micro-dystrophin gene under the control of a muscle specific promoter

Recombinant adeno-associated viral vector encoding a human micro-dystrophin gene under the control of a muscle specific promoter
Trade Name
Orphan Indication Duchenne muscular dystrophy
EU Market Approval EU
EU Designation Date 2016-10-14 00:00:00
Sponsor Pharma Gateway AB