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recombinant adeno-associated virus serotype 9 vector containing the transgene UBE3A encoding for ubiquitin protein ligase E3A/E6-AP |
|---|---|
| Trade Name | |
| Orphan Indication | Angelman syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2015-10-29 00:00:00 |
| Sponsor | Agilis Biotherapeutics, LLC;245 First Street, Suite 1800;Cambridge, Massachusetts, 02142 |
