Trial Readiness and Endpoint Assessment in LGMD R1

Limb-girdle muscular dystrophy type 2A

Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I) Trial Readiness and Endpoint Assessment in LGMD R1 A Phase 1/2 Dose-escalation Study to Evaluate the Safety of LION-101 in Adult Subjects With Genetic Confirmation of LGMD2I/R9 (Part1) 3 Year Follow up on ANO5 Patients Limb-Girdle Muscular Dystrophy Type 2I in Norway A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I) MRI and Muscle Involvement in Patients With Mutations in GMPPB Fast Troponin as a Biomarker to Assess Exercise-induced Muscle Damage in Muscle Diseases Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I Natural History of Limb Girdle Muscular Dystrophy Type 2A and Type 2E MRI on Persons With Mutations in POMT2 Gene (LGMD2N) Biomarker Development in LGMD 2i