adeno-associated virus (AAV) serotype rh.10 expressing beta-galactosidase | |
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Trade Name | |
Orphan Indication | Gangliosidosis generalized GM1- type 1 |
USA Market Approval | USA |
USA Designation Date | 2017-01-30 00:00:00 |
Sponsor | Lysogene, Inc.;245 First Street, 18th Floor;Cambridge, Massachusetts, 02142 |