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an adeno-associated viral vector containing a codon-optimised human factor IX gene (AAV5-hFIXco) |
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| Trade Name | |
| Orphan Indication | Hemophilia B |
| USA Market Approval | USA |
| USA Designation Date | 2011-12-22 00:00:00 |
| Sponsor | uniQure, B.V.;Meiberdreef 61, 1100 DA;Amsterdam |
