|
adeno-associated viral vector containing modified U11 snRNA |
|---|---|
| Trade Name | |
| Orphan Indication | Duchenne muscular dystrophy |
| USA Market Approval | USA |
| USA Designation Date | 2010-09-15 00:00:00 |
| Sponsor | uniQure Biopharma B.V.;Paasheuvelweg 25, 1105 BP;Amsterdam |
|
adeno-associated viral vector containing modified U11 snRNA |
|---|---|
| Trade Name | |
| Orphan Indication | Duchenne muscular dystrophy |
| USA Market Approval | USA |
| USA Designation Date | 2010-09-15 00:00:00 |
| Sponsor | uniQure Biopharma B.V.;Paasheuvelweg 25, 1105 BP;Amsterdam |