Exon 46 specific phosphorothioate oligonucleotide

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Exon 46 specific phosphorothioate oligonucleotide
Trade Name
Orphan Indication Duchenne muscular dystrophy
USA Market Approval USA
USA Designation Date 2005-11-18 00:00:00
Sponsor Prosensa Therapuetics BV;J. H. Oortweg, 2333 CH;Leiden
Related Access Program
PTC Therapeutics – Duchenne Muscular Dystrophy Marathon Pharmaceuticals, LLC. – Duchenne muscular dystrophy PTC Therapeutics International Limited – Duchenne muscular dystrophy