|
2′-O-methyl phosphorothioate 5′-GCUAGGUUUACGGGACCUCU-3′ |
|---|---|
| Trade Name | |
| Orphan Indication | Amyotrophic lateral sclerosis |
| USA Market Approval | USA |
| USA Designation Date | 2012-10-31 00:00:00 |
| Sponsor | LifeSplice Pharma LLC;1 Great Valley Parkway, Suite 20;Malvern, Pennsylvania, 19355 |
